Thanks to Sharktank and their work with non sense mutations!
PTC Therapeutics' ataluren fails late-stage study in patients with nonsense mutation cystic fibrosis
Since we got the sad news that Ataluren failed in the late stage study...we have some good news:
Indrepta, a nutritional supplement for non sense mutations, is now on the market!
Jim Caldwell and the Sharktank group are doing amazing work getting new supplements to our community.
Jim has helped us in many ways here at the forums with his expertise in IT too. We are grateful!
Salt and Light,
Has anyone tried this yet or is there some study showing results?
I'm intrigued and sent the info to my doc for their opinion.