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  1. PTC124
  2. PTC124
  3. PTC124
  4. Great News on PTC124
  5. VX-770
  6. PTC124
  7. PTC124
  8. VX-770 (Vertex Pharmaceuticals, Inc.)
  9. PTC124
  10. PTC124
  11. Any news regarding PTC124?
  12. VX-770
  13. Vx 770.
  14. VX-770
  15. PTC-124 articles
  16. New info on PTC124
  17. G551D -VX770
  18. PTC124 for Nonsense Mutations
  19. PTC124
  20. Positive News About VX-770 and CF Patient Assistance Foundation
  21. VX-770
  22. PTC124 for Nonsense Mutations
  23. VX-809 for DDF508
  24. Denufasol vs VX potentiator (VX-770?)
  25. PTC 124
  26. PTC 124
  27. Encouraging Interview/Article about VX-770 and VX-809
  28. VX-770
  29. PTC Moving to phase III
  30. VX-770 Update
  31. The future witha VX drug
  32. VX-770 and Delta f508
  33. What will VX-809 do for me?
  34. PTC124 (Ataluren)
  35. VX-770 Updates
  36. Open label for VX 770
  37. VX 770
  38. Any PTC124 (atalurens) out there?
  39. updates on vx770 and 809
  40. drug study combining the two VX drugs
  41. Ataluren (PTC124) Are study participants close to finishing?
  42. PTC 124 (Ataluren)
  43. Children doing the PTC 124 trial
  44. vx770 trial results
  45. VX770/809
  46. Can you just go up and buy Ataluren (PTC 124)
  47. VX 770 combined with VX 809
  48. vx770 and vx809
  49. Recruitment for VX combined
  50. > > March 29, 2011 11:30 UTC > > Phase 3 Study of VX-770 in Children Ages 6 to 11
  51. vx770
  52. VX 770-will it help us?
  53. vx-661
  54. VX-770 tablets
  55. ataluren
  56. VX 770 on clinical trial website
  57. VX-770 to be 250K p/year per patient
  58. FDA VX-770
  59. VX -770 for Australians
  60. Vx-770 and Disability Review
  61. VX770
  62. VX 770 and CFRD
  63. New Trial for the drug VX-809, delta 508
  64. Kalydeco question
  65. vx770 for some other mutations!
  66. New drug--Kalydeco--Approved
  67. G551d kalydeco/vx770
  68. Vx-770 and hemoptysis
  69. Kalydeco - insurance approval?
  70. DF508ers who participated in VX-770 trials
  71. vertex770 and class IV
  72. 809/770
  73. To those on kalydeco---Lauren (your thoughts, please)
  74. 809
  75. Interesting info about VX770
  76. Information for people in Australia waiting for Kalydeco
  77. Kalydeco cost
  78. vx-661 recruiting
  79. Anybody have any information about Vertex 661?
  80. Kalydeco - side effects
  81. CF GeneE App by Vertex!
  82. 809 Trial
  83. Does anyone know if Kalydeco would work or can be tried on other mutation?
  84. I am f508 and 3272-26a>g. How do I know if mine is gating and what class I'm in?? Darryl 44 dx 24
  85. Good website explaining CFTR and many of it's associations
  86. Article: Fix two defects to combat cystic fibrosis
  87. TOCRIS Bioscience
  88. 661 & 770 recruiting
  89. What is a 7t-9t variance
  90. Anyone on Kayldeco and not G551D? Is it helping?
  91. Kalydeco or VX-770 off lable use?
  92. Saveferris 2009
  93. Genotyping, John's Hopkin's research
  94. Largest gene therapy trial for cystic fibrosis begins
  95. G551D mutation and results from starting Kalydeco
  96. DF508 and Kalydeco
  97. Effecacy of Kalydeco: Pancreatic sufficiency as an indicator?
  98. Kalydeco for Australians
  99. Collecting data for homozygous Delta508
  100. Getting a script for Kalydeco if you are not G551D
  101. Kalydeco & low lung function.
  102. Bad news from Vertex
  103. Just so frustrated! *Vent*
  104. Kalydeco side effects
  105. If you don't have a gating mutation and want Kalydeco....
  106. kalydeco & 70% fev1?
  107. Email address for Vertex
  108. Insights from current 661 or 809 trials
  109. vx 661 discussion moved
  110. 809/661 thread not working
  111. Vertex 809 trial
  112. My first update since starting Kalydeco
  113. G551D Australian coming to the US for Ivacaftor (Kalydeco)
  114. Do you have update on how the phase 2 trial is doing.
  115. Do you know any information on phase2Trial
  116. Off Label Kalydeco
  117. DF508 question
  118. Kalydeco off-label: My first 4 days
  119. Missing posts
  120. Corrector
  121. two weeks on kalydeco!
  122. CFTR2 Site is now active
  123. thread cut off
  124. link for additional info on more mutations that may benefit from Ivacaftor
  125. v520f
  126. Forbes series on FDA process
  127. g551d mutations on Kalydeco
  128. Off Label Kalydeco-My follow up Appt.
  129. Kalydeco
  130. Anyone on Kalydeco seen changes in LFT's?
  131. ataluren
  132. To Those on Kalydeco
  133. Kalydeco
  134. link from FB
  135. VX 809/770 Phase 2 interim results - 5-10% improvement in lung function
  136. VX 770 / VX 809 / VX 661
  137. Forbes article
  138. Kalydeco Medicine
  139. Any Canadians on here?
  140. Why Kalydeco may work for a larger population
  141. G551D patients on Kalydeco
  142. Kalydeco - liver enzymes are elevated *UPDATE*
  143. Kalydeco and Class IV Mutations
  144. More about Kalydeco and other mutations
  145. Vertex news release
  146. Kalydeco in Australia Update
  147. Does Kalydeco help you stay healthy?
  148. Normal Liver Enzymes after 10 weeks on Kaly
  149. 770+809 clarification
  150. Atalauren
  151. Ataluren being announced today at European cf conference
  152. update on finding of Ataluren FDA approval
  153. Anyone with DF508 and M1101R?
  154. Interpretation of Ataluren Press Release
  155. New clinical trials with Kalydeco
  156. DF508 & 1248 + 1 G>A
  157. Third check in after Kalydeco
  158. Dr agreed to give off label prescription for Kalydeco
  159. It is possible to get Kalydeco in Canada
  160. APPROVED!!!!!
  161. Will this mean a P-III???
  162. KALYIDECO-
  163. Starting Kalydeco Today
  164. Final phase 2 results
  165. How do you volunteer for the VX809 phase III trial
  166. Abby Update
  167. Off Label Kalydeco Question
  168. Expanded Access/compassionate use
  169. Kalydeco may help COPD
  170. Sweat test result and menstrual cycle
  171. D508/R117 mutations
  172. Abby Sweat Tests
  173. Kalydeco users help needed
  174. questions about therapies for g551ds, who are on Kalydeco
  175. Abby update
  176. Kalydeco gets EMA approval (Europe) & Vertex has applied to the TGA (Australia) and the TPD (Canada)
  177. DF508 and ??
  178. Double DF508
  179. For those on Kalydeco--help those in UK and Ireland
  180. PTC 124 updates?
  181. Kalydeco non G551D users
  182. Kalydeco and cataracts
  183. Pregnancy and Kalydeco
  184. Cys866Tyr or Cystic Fibrosis Variant?
  185. CFTR diagnosis Vs CF diagnosis
  186. c.1210-12T 5T mutation
  187. Abby Great update!!
  188. V520f mutation
  189. V520f
  190. Ivacaftor and splicing mutations..
  191. New trial with Kalydeco and splicing/residual function mutations
  192. Can sweat chloride numbers drop on their own?
  193. How to tell what trials or medicines may apply to mutations?
  194. Gene Therapy Removed from Drug Pipeline
  195. Another Great Abby Update!!!
  196. New to pancreatic enzymes
  197. 809 combo study -- full data release
  198. New Facebook Group for Canadians Interested in Kalydeco
  199. DF508 and S489x? Anyone with this?
  200. Phase III Combo 809/770
  201. This is really cool!! More possible cure prospects!!
  202. Sweat Tests
  203. THE ROLE OF THE BRITISH GOVERNMENT in respect of VERTEX.
  204. Glybera - Gene Therapy
  205. CFFT Announces $58 Million CF Drug Discovery Agreement with PFIZER
  206. treatment of CF patients low doses of amitriptyline
  207. Vest use for a 2 yr old
  208. VX-770 Study on Class 3 mutations...
  209. Cystic fibrosis patients could soon benefit from breakthrough small-molecule drugs
  210. Regulation of CFTR gating (normal and CF)
  211. Channel activators (potentiators) of cystic fibrosis (CF) transmembrane conductance r
  212. Abby update
  213. Good News from England
  214. F508del and 2184insA
  215. Have Any DF508's Started the Third Phase of Trials Yet?
  216. DDF508 & Kalydeco~ Anyone in any of the trials with these mutations, experiences?
  217. Kalyedeco and or VX-770/809 experiences- Please share
  218. F508Del and M470V
  219. Difference between VX-661/VX-770 and VX-809/VX-770 study
  220. What is a 1 to N trial
  221. 809 + 770 Phase 3 announced
  222. How is it for the F508del?
  223. Info for people on Kalydeco: why fat is needed and medications that interact
  224. no changes on Kalydeco
  225. Kalydeco + D579G
  226. buying kalydeco overseas
  227. N30 phase 1b/2a trial with CFs who have 2 copies of F508del
  228. New gene therapy theory/new vector idea please look even if it is wrong
  229. Luminex launched new cystic fibrosis test
  230. How can we make the pipeline go faster?
  231. Phase 2 VX661/Kalydeco results released
  232. how do i know?
  233. Question about F1052V and Drugs on the Pipeline
  234. Vertex drugs and pancreatic function
  235. Galapagos: New CFTR Potentiator
  236. Kalydeco and Insurance
  237. Cystic Fibrosis: Charity and Industry Partner for Profit - article from medpage today
  238. Anyone can please tell me about strep throat symptoms??
  239. New to this forum
  240. Latest Vertex News: New data for F508del and G551D
  241. Ataluren Update
  242. Abby Clinic Update
  243. New Drugs and insulin use
  244. Today show and Kalydeco
  245. V520f
  246. Looking for anyone who has tried to get Kalydeco off label
  247. Australian wanting to get Kalydeco from USA or UK (or anywhere!)
  248. Elvated ALT levels
  249. Vertex Update: New data for other gating mutations and new trial for G551D
  250. 809 vs 661